This Presentation will address:
- Platform vector gene therapy (PaVe-GT) approach for rare diseases,
- Translational development for the four AAV gene therapies in PaVe-GT: pathway and current status, as well as,
- Challenges and potential solutions
…with Q&A to follow
Please log on for the next Topics in Clinical Research meeting on February 21st, 2024 via Microsoft Teams (link provided below) where we welcome Rodica Stan, Ph.D., Senior Scientific Project Manager Therapeutic Development Branch, National Center for Advancing Translational Sciences, Division of Preclinical Innovation as she presents on AAV-Based Gene Therapy Development.
Dr. Rodica Stan is a Senior Scientific Project Manager in the Therapeutic Development Branch within NCATS' Division of Preclinical Innovation, where she manages gene therapy and small–molecule projects for rare and ultra-rare diseases, with the objective of moving therapies efficiently through Investigational New Drug-enabling studies, regulatory reviews and clinical testing. She has accumulated experience and expertise in translational research, working for more than 15 years on academic and industry projects at Memorial Sloan-Kettering Cancer Center (New York, NY), the Ludwig Institute for Cancer Research (Melbourne, Australia), and City of Hope (Duarte, CA). Dr. Stan managed translational projects — specifically in cell and gene therapy in oncology and HIV/AIDS — expanding to small molecules and vaccines for other diseases.
-------------------------------------------------
Microsoft Teams meeting
Click here to join the meeting
Meeting ID: 266 432 775 330
Passcode: AJFN8G
Or call in (audio only)
Phone Conference ID: 192 783 517#
------------------------------------------------
CONTACTS
Name: Sandi Bonifant
Email: bonifans@ninds.nih.gov
Phone: 301-451-0867
Or
Name: Katy Finnell
Email: finnellk@nih.gov
Phone: 301-594-3359